Topics Featured in the Presentation:

• Introduction to Dystrophin
• Class of Therapies:
  • Exon Skipping Therapy
  • Gene Transfer Therapy
  • Small Molecule Therapy
  • Glucocorticoids
  • Immunotherapy
  • Cell-based Therapy
• Case-based Discussion

Upon completion of the activity, participants should be able to:

• Describe the role of dystrophin disruption and restoration in the progression and management of DMD
• Assess the latest clinical trial results across various treatment modalities for DMD
• Examine emerging approaches to DMD management that seek to align patient selection, treatment choice, and optimal initiation of therapy

This activity is provided by The France Foundation.

In support of improving patient care, this activity has been planned and implemented by The France Foundation. The France Foundation is jointly accredited by the Accreditation Council for Continuing Medical Education (ACCME), the Accreditation Council for Pharmacy Education (ACPE), and the American Nurses Credentialing Center (ANCC) to provide continuing education for the healthcare team.

Physicians: The France Foundation designates this enduring activity for a maximum of 1.0 AMA PRA Category 1 Credit(s)™. Physicians should claim only the credit commensurate with the extent of their participation in the activity.

Nurses: The France Foundation designates this activity for 1.0 nursing contact hours.

Pharmacists
This knowledge-based activity, UAN # JA0007204-0000-24-001-L01-P, qualifies for 1.0 contact hours (0.10 CEUs) of continuing pharmacy education credit. Please submit all evaluations and credit requests no later than 30 days after you complete this activity to ensure your credit fulfillment, as CE credit cannot be awarded past 60 days from the activity date. Your CE credits will be electronically submitted to the NABP upon successful completion of the activity. Pharmacists with questions can contact NABP customer service at custserv@nabp.net.

Physician Assistants: The France Foundation has been authorized by the American Academy of PAs (AAPA) to award AAPA Category 1 CME credit for activities planned in accordance with AAPA CME Criteria. This activity is designated for 1.0 AAPA Category 1 CME credits. PAs should only claim credit commensurate with the extent of their participation.

All other healthcare professionals completing this course will be issued a statement of participation.

This activity is supported by an independent medical educational grant from Sarepta Therapeutics.

Not an official event of the 2024 MDA Clinical & Scientific Conference. Not sponsored, endorsed, or accredited by MDA.